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Research

  1. Home
  2. Posts tagged"Research"
Azafaros press release:  Azafaros announces positive topline Phase 2 study data with nizubaglustat in GM2 gangliosidosis and Niemann-Pick disease type C
16 Jul
DanielLewi0 Comments

Azafaros press release:  Azafaros announces positive topline Phase 2 study data with nizubaglustat in GM2 gangliosidosis and Niemann-Pick disease type C

We are pleased to share the latest press release from Azafaros related
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Sanofi Press Release: Sanofi’s AMETHIST trial for GM2 gangliosidosis discontinued
25 Apr
DanielLewi0 Comments

Sanofi Press Release: Sanofi’s AMETHIST trial for GM2 gangliosidosis discontinued

Today it was announced by Sanofi that the AMETHIST phase 3 study of venglustat
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Azafaros RAINBOW study update: Completion of 12 week phase 2
12 Mar
DanielLewi0 Comments

Azafaros RAINBOW study update: Completion of 12 week phase 2

Azafaros has just announced the successful completion of its 12-week Phase 2
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Patient-Focused Drug Development (PFDD) meeting with the FDA for GM2 Gangliosidosis 
22 Jan
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Patient-Focused Drug Development (PFDD) meeting with the FDA for GM2 Gangliosidosis 

Our friends at the National Tay-Sachs & Allied Diseases Association have been
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WORLDSymposium 2021 poster
15 Mar
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WORLDSymposium 2021 poster

In February 2021 we were delighted to present our latest poster alongside
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National Organization for Rare Disorders (NORD) Summit 2020 Poster
15 Mar
DanielLewi0 Comments

National Organization for Rare Disorders (NORD) Summit 2020 Poster

In October 2020 we were delighted to present alongside our registry partners
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Intrabio IB1001-202 Clinical Trial
15 Mar
DanielLewi0 Comments

Intrabio IB1001-202 Clinical Trial

The FAQ and clinical trial brochure for the Intrabio IB1001-202 trial can
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NOW Enrolling: GM2 gangliosidosis Gene Therapy Clinical Trial at Queens University
15 Mar
DanielLewi0 Comments

NOW Enrolling: GM2 gangliosidosis Gene Therapy Clinical Trial at Queens University

Global enrollment is now open for the TSHA-101 clinical trial at Queens
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IB1001 Ongoing, Multinational Clinical Trials update
21 Oct
DanielLewi0 Comments

IB1001 Ongoing, Multinational Clinical Trials update

IntraBio is currently conducting three clinical trials with its lead compound IB1001 (N-acetyl-L-leucine) across
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