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Azafaros press release: Azafaros announces positive topline Phase 2 study data with nizubaglustat in GM2 gangliosidosis and Niemann-Pick disease type C
We are pleased to share the latest press release from Azafaros related
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Sanofi Press Release: Sanofi’s AMETHIST trial for GM2 gangliosidosis discontinued
Today it was announced by Sanofi that the AMETHIST phase 3 study of venglustat
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Azafaros RAINBOW study update: Completion of 12 week phase 2
Azafaros has just announced the successful completion of its 12-week Phase 2
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Patient-Focused Drug Development (PFDD) meeting with the FDA for GM2 Gangliosidosis
Our friends at the National Tay-Sachs & Allied Diseases Association have been
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WORLDSymposium 2021 poster
In February 2021 we were delighted to present our latest poster alongside
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National Organization for Rare Disorders (NORD) Summit 2020 Poster
In October 2020 we were delighted to present alongside our registry partners
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Intrabio IB1001-202 Clinical Trial
The FAQ and clinical trial brochure for the Intrabio IB1001-202 trial can
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NOW Enrolling: GM2 gangliosidosis Gene Therapy Clinical Trial at Queens University
Global enrollment is now open for the TSHA-101 clinical trial at Queens
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IB1001 Ongoing, Multinational Clinical Trials update
IntraBio is currently conducting three clinical trials with its lead compound IB1001 (N-acetyl-L-leucine) across
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